Elamipretide
4 research papers indexed
Karaa 2018 — Elamipretide Dose-Escalation Trial in Primary Mitochondrial Myopathy
188
Neurology
·2018Clinical TrialHumanPrimary mitochondrial myopathySourceClinical Trial
Thompson 2021 — Elamipretide Phase 2/3 Barth Syndrome Trial
133
Genetics in Medicine
·2021Clinical TrialHumanBarth syndromeSourceClinical Trial
Karaa 2023 — MMPOWER-3 Elamipretide Randomized Clinical Trial
72
Neurology
·2023RCTHumanPrimary mitochondrial myopathySourceRCT
Thompson 2024 — TAZPOWER 168-Week Open-Label Elamipretide Extension
42
Genetics in Medicine
·2024Open LabelHumanBarth syndromeSourceOpen Label